Researchers at the University of Basel have developed a gene therapy that could potentially treat a rare and currently fatal ...

Edgewise Therapeutics, Inc. (Nasdaq: EWTX), a leading muscle disease biopharmaceutical company, today announced its participation at the 2026 Muscular Dystrophy Association (MDA) Clinical and ...

More than 30 rare muscular dystrophy types cause progressive muscle weakness from inherited gene mutations. Combined, they affect about 1 in 5,000 to 8,000 people. Common subtypes vary by age of onset ...

Columnist Patrick Moeschen turns to classic writers and poets to express how he is choosing hope in life with limb-girdle muscular dystrophy.

BELIEVE WHAT HAPPENED NEXT. FOUR YEAR OLD LUCAS LOVES A GOOD PLAYDATE AT THE PARK. HI, LUCAS. HI. IT’S SANDBOX TRUCKS TODAY, BUT HIS FAVORITE PLAYING SUPERHEROES. THIS IS HIS FAVORITE RIGHT NOW. PJ ...

Muscular dystrophy came for my vision first, although I did not know it at the time. On the second Friday morning of April 2020, I realized quite suddenly I couldn’t read out of my right eye. I could ...

Delandistrogene moxeparvovec, a gene therapy for Duchenne muscular dystrophy (DMD), showed high dystrophin expression and a favorable safety profile in young patients. Delandistrogene moxeparvovec ...

AI-ECG provides a non-invasive, accessible alternative for detecting LVSD in muscular dystrophy patients, overcoming challenges of routine echocardiography. The study showed AI-ECG's high sensitivity ...

ST. LOUIS — As far as 10-year-old Dean Alesi is concerned, the best gift his parents ever gave him was his little brother. "Dean has wanted a brother or sister since he was like 3 or 4," his mom Amber ...

A cell therapy stabilizes weakened muscles -- including the heart muscle -- in Duchenne muscular dystrophy patients, a new study shows. A cell therapy developed by the executive director of the Smidt ...