Reading genetic activity from living cells without destroying them

Until now, studying the genetic processes in cells required destroying them—making it impossible to observe these processes ...
Scientific American

How scientists made the discoveries behind a game-changing gene therapy for sickle cell disease

Stuart Orkin and Swee Lay Thein shared a Breakthrough Prize in Life Sciences for their research on genetic causes of sickle ...
Scientific American

How a vision-restoring gene therapy proved that we can treat inherited diseases

Three 2026 Breakthrough Prize winners reflect on developing Luxturna, a gene therapy that treats blindness caused by rare ...

Many genes have been linked to autism—but a new study suggests it may be their path to the brain that matters

In recent years, scientists have identified hundreds of different genes associated with autism, a burst of discovery that has ...
Science Daily

Scientists found the “holy grail” gene that could one day help humans regrow limbs

Scientists studying axolotls, zebrafish, and mice have uncovered a shared set of genes that may one day help humans regrow ...
Science Daily

Scientists successfully transfer longevity gene and extend lifespan

Scientists at the University of Rochester pulled off a remarkable experiment: they transferred a longevity-related gene from ...

FDA approves first gene therapy for inherited deafness, shown to restore hearing for children with rare condition

The US Food and Drug Administration on Thursday approved the first gene therapy for inherited hearing loss, a one-time treatment that proved to be life-changing for a small number of children in a ...